The prevalence rates of metabolic dysfunction–associated steatohepatitis (MASH) and metabolic dysfunction–associated ...
Imagine a future where your doctor can tailor your treatment based on your unique genetic make-up and predict and prevent ...
Spinal muscular atrophy (SMA) is a rare hereditary neuromuscular disorder in which the spinal cord does not form normally.
Because sickle cell disease isn’t as progressive a disease as others that have gene therapies available, there isn’t as much ...
The babies were treated before symptom onset, and are sitting, standing, and walking independently, many consistent with ...
This week will see the return of the Assisted Dying Bill to Parliament, as it is formally introduced to the House of Commons.
Two years after treatment, both girls show normal motor function and no signs of spinal muscular atrophy symptoms.
The biotechnology industry is rapidly evolving, with innovative companies pushing the boundaries of science and medicine. To ...
Dr Patricia Ares-Romero and Dr Martin Rosenzweig discuss treatment strategies for TRD, including alternative therapies and explain current barriers within the healthcare system that inhibit access.
Majority of children with SMA treated with Roche’s Evrysdi are able to sit, stand and walk independently, two-year data demonstrate ...
Analyst Jason Gerberry of Bank of America Securities maintained a Buy rating on Biohaven Ltd. (BHVN – Research Report), retaining the ...
The findings are significant for the liver research community and others interested in the gut-liver axis. (A) AOAH cleaves the two piggyback fatty acyl chains from the lipid A moiety, inactivating ...