An experimental immunotherapy has beaten aggressive brain tumours in a handful of children, and a personalised version is now ...
TAA-T cell therapy left four children with terminal brain cancer in long-term remission, with two new trials now expanding ...
In utero gene therapy uses prenatal genetic screening to identify fetuses with lethal mutations and delivers corrective genes ...
Add Yahoo as a preferred source to see more of our stories on Google. Gene editing fixed brain mutations in mice with AHC, offering hope for treating rare neurological diseases at the DNA level.
Researchers are exploring delivering super-specific AAVs through the brain's natural waste disposal system, which can carry ...
Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. The Food and Drug Administration paused ...
A first-in-human cell therapy trial at Children's National produced four long-term survivors in children with terminal DIPG ...